Efficacy of sapropterin dihydrochloride (tetrahydrobiopterin, 6R-BH4) for reduction of phenylalanine concentration in patients with phenylketonuria: a phase III randomised placebo-controlled study-Reference-Cited by-同舟云学术

Efficacy of sapropterin dihydrochloride (tetrahydrobiopterin, 6R-BH4) for reduction of phenylalanine concentration in patients with phenylketonuria: a phase III randomised placebo-controlled study

Published:2007-08 Issue:9586 Volume:370 Page:504-510
ISSN:0140-6736
Container-title:The Lancet
language:en
Short-container-title:The Lancet

Author:

Levy Harvey L,Milanowski Andrzej,Chakrapani Anupam,Cleary Maureen,Lee Philip,Trefz Friedrich K,Whitley Chester B,Feillet François,Feigenbaum Annette S,Bebchuk Judith D,Christ-Schmidt Heidi,Dorenbaum Alex

Publisher

Elsevier BV

Subject

General Medicine

Reference38 articles.

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2. Phenylketonuria: epitome of human biochemical genetics (first of two parts);Scriver;N Engl J Med,1980

3. Hyperphenylalaninemia: phenylalanine hydroxylase deficiency. Chapter 77;Donlon,2004

4. Phenylketonuria in adulthood: a collaborative study;Koch;J Inherit Metab Dis,2002

5. Blood phenylalanine control in adolescents with phenylketonuria;Walter;Int J Adolesc Med Health,2004

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