Safety and efficacy of alternative alglucosidase alfa regimens in Pompe disease-Reference-Cited by-同舟云学术

Safety and efficacy of alternative alglucosidase alfa regimens in Pompe disease

Published:2015-04 Issue:4 Volume:25 Page:321-332
ISSN:0960-8966
Container-title:Neuromuscular Disorders
language:en
Short-container-title:Neuromuscular Disorders

Author:

Case Laura E.^ORCID,Bjartmar Carl,Morgan Claire,Casey Robin,Charrow Joel,Clancy John P.,Dasouki Majed,DeArmey Stephanie,Nedd Khan,Nevins Mary,Peters Heidi,Phillips Dawn,Spigelman Zachary,Tifft Cynthia,Kishnani Priya S.

Funder

Genzyme

Publisher

Elsevier BV

Subject

Genetics(clinical),Clinical Neurology,Neurology,Pediatrics, Perinatology, and Child Health

Reference21 articles.

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2. Towards a molecular therapy for glycogen storage disease type II (Pompe disease);Chen;Mol Med Today,2000

3. Early treatment with alglucosidase alpha prolongs long-term survival of infants with Pompe disease;Kishnani;Pediatr Res,2009

4. Myozyme (alglucosidase alfa) [package insert],2012

5. Recombinant human acid [alpha]-glucosidase: major clinical benefits in infantile-onset Pompe disease;Kishnani;Neurology,2007

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