Early Treatment With Alglucosidase Alfa Prolongs Long-Term Survival of Infants With Pompe Disease-Reference-Cited by-同舟云学术

Early Treatment With Alglucosidase Alfa Prolongs Long-Term Survival of Infants With Pompe Disease

Published:2009-09 Issue:3 Volume:66 Page:329-335
ISSN:0031-3998
Container-title:Pediatric Research
language:
Short-container-title:Pediatr Res

Author:

Kishnani Priya S,Corzo Deya,Leslie Nancy D,Gruskin Daniel,van der Ploeg Ans,Clancy John P,Parini Rosella,Morin Gilles,Beck Michael,Bauer Mislen S,Jokic Mikael,Tsai Chen-En,Tsai Brian W H,Morgan Claire,O'Meara Tara,Richards Susan,Tsao Elisa C,Mandel Hanna

Publisher

Springer Science and Business Media LLC

Subject

Pediatrics, Perinatology and Child Health

Reference20 articles.

1. Glycogen storage disease types I and II: Treatment updates

2. Pompe disease in infants and children

3. Towards a molecular therapy for glycogen storage disease type II (Pompe disease)

4. The Natural Course of Infantile Pompe’s Disease: 20 Original Cases Compared With 133 Cases From the Literature

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