Targeted Exon Skipping Restores Type VII Collagen Expression and Anchoring Fibril Formation in an In Vivo RDEB Model
Author:
Publisher
Elsevier BV
Subject
Cell Biology,Dermatology,Molecular Biology,Biochemistry
Reference46 articles.
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1. Splice modulation strategy applied to deep intronic variants in COL7A1 causing recessive dystrophic epidermolysis bullosa;Proceedings of the National Academy of Sciences;2024-08-19
2. Emerging DNA & RNA editing strategies for the treatment of epidermolysis bullosa;Journal of Dermatological Treatment;2024-08-18
3. Is Exon Skipping a Viable Therapeutic Approach for Vascular Ehlers–Danlos Syndrome with Mutations in COL3A1 Exon 10 or 15?;International Journal of Molecular Sciences;2024-08-13
4. Efficacy, biodistribution and safety comparison of chemically modified antisense oligonucleotides in the retina;Nucleic Acids Research;2024-08-09
5. Twin Prime Editing Mediated Exon Skipping/Reinsertion for Restored Collagen VII Expression in Recessive Dystrophic Epidermolysis Bullosa;Journal of Investigative Dermatology;2024-05
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