Twin Prime Editing Mediated Exon Skipping/Reinsertion for Restored Collagen VII Expression in Recessive Dystrophic Epidermolysis Bullosa-Reference-Cited by-同舟云学术

Twin Prime Editing Mediated Exon Skipping/Reinsertion for Restored Collagen VII Expression in Recessive Dystrophic Epidermolysis Bullosa

Published:2024-05 Issue: Volume: Page:
ISSN:0022-202X
Container-title:Journal of Investigative Dermatology
language:en
Short-container-title:Journal of Investigative Dermatology

Author:

Steinbeck Benjamin J.^ORCID,Gao Xin D.^ORCID,McElroy Amber N.^ORCID,Pandey Smriti^ORCID,Doman Jordan L.^ORCID,Riddle Megan J.^ORCID,Xia Lily^ORCID,Chen Weili^ORCID,Eide Cindy R.^ORCID,Lengert Andre H.^ORCID,Han Sang Won^ORCID,Blazar Bruce R.^ORCID,Wandall Hans H.^ORCID,Dabelsteen Sally^ORCID,Liu David R.^ORCID,Tolar Jakub^ORCID,Osborn Mark J.^ORCID

Publisher

Elsevier BV

Reference73 articles.

1. Programmable deletion, replacement, integration and inversion of large DNA sequences with twin prime editing;Anzalone;Nat Biotechnol,2022

2. Search-and-replace genome editing without double-strand breaks or donor DNA;Anzalone;Nature,2019

3. Engineered virus-like particles for efficient in vivo delivery of therapeutic proteins;Banskota;Cell,2022

4. STRAIGHT-IN enables high-throughput targeting of large DNA payloads in human pluripotent stem cells;Blanch-Asensio;Cell Rep Methods,2022

5. Clinically relevant correction of recessive dystrophic epidermolysis bullosa by dual sgRNA CRISPR/Cas9-mediated gene editing;Bonafont;Mol Ther,2019

Cited by 2 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Nucleic Acid Therapy for the Skin;Journal of Investigative Dermatology;2024-09

2. Emerging DNA & RNA editing strategies for the treatment of epidermolysis bullosa;Journal of Dermatological Treatment;2024-08-18