Editing the Sickle Cell Disease Mutation in Human Hematopoietic Stem Cells: Comparison of Endonucleases and Homologous Donor Templates-Reference-Cited by-同舟云学术

Editing the Sickle Cell Disease Mutation in Human Hematopoietic Stem Cells: Comparison of Endonucleases and Homologous Donor Templates

Published:2019-08 Issue:8 Volume:27 Page:1389-1406
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Romero Zulema,Lomova Anastasia,Said Suzanne,Miggelbrink Alexandra,Kuo Caroline Y.,Campo-Fernandez Beatriz,Hoban Megan D.,Masiuk Katelyn E.,Clark Danielle N.,Long Joseph,Sanchez Julie M.,Velez Miriam,Miyahira Eric,Zhang Ruixue,Brown Devin,Wang Xiaoyan,Kurmangaliyev Yerbol Z.,Hollis Roger P.,Kohn Donald B.

Funder

Doris Duke Charitable Foundation

California Institute for Regenerative Medicine

QCB Collaboratory Postdoctoral Fellowship

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference50 articles.

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2. Targeted genome editing in human repopulating haematopoietic stem cells;Genovese;Nature,2014

3. Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells;Hoban;Blood,2015