COL7A1 Editing via CRISPR/Cas9 in Recessive Dystrophic Epidermolysis Bullosa-Reference-Cited by-同舟云学术

COL7A1 Editing via CRISPR/Cas9 in Recessive Dystrophic Epidermolysis Bullosa

Published:2017-11 Issue:11 Volume:25 Page:2573-2584
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Hainzl Stefan,Peking Patricia,Kocher Thomas,Murauer Eva M.,Larcher Fernando,Del Rio Marcela,Duarte Blanca,Steiner Markus,Klausegger Alfred,Bauer Johann W.,Reichelt Julia,Koller Ulrich

Funder

DEBRA Austria

MINECO

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference46 articles.

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2. Site-specific genome editing for correction of induced pluripotent stem cells derived from dominant dystrophic epidermolysis bullosa;Shinkuma;Proc. Natl. Acad. Sci. U S A,2016

3. Clinical translation of TALENS: treating SCID-X1 by gene editing in iPSCs;Biffi;Cell Stem Cell,2015

4. Gene editing of CCR5 in autologous CD4 T cells of persons infected with HIV;Tebas;N. Engl. J. Med.,2014

5. Human COL7A1-corrected induced pluripotent stem cells for the treatment of recessive dystrophic epidermolysis bullosa;Sebastiano;Sci. Transl. Med.,2014

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2. Emerging DNA & RNA editing strategies for the treatment of epidermolysis bullosa;Journal of Dermatological Treatment;2024-08-18

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5. Establishment of a Cleavage-Based Single-Plasmid Dual-Luciferase Surrogate Reporter for the Cleavage Efficiency Evaluation of CRISPR-Cas12a Systems and Its Primary Application;The CRISPR Journal;2024-06-01