Human COL7A1 -corrected induced pluripotent stem cells for the treatment of recessive dystrophic epidermolysis bullosa-Reference-Cited by-同舟云学术

Human COL7A1 -corrected induced pluripotent stem cells for the treatment of recessive dystrophic epidermolysis bullosa

Published:2014-11-26 Issue:264 Volume:6 Page:
ISSN:1946-6234
Container-title:Science Translational Medicine
language:en
Short-container-title:Sci. Transl. Med.

Author:

Sebastiano Vittorio¹²,Zhen Hanson Hui³,Haddad Bahareh¹,Bashkirova Elizaveta¹,Melo Sandra P.³,Wang Pei⁴,Leung Thomas L.⁴,Siprashvili Zurab³,Tichy Andrea³,Li Jiang³,Ameen Mohammed³,Hawkins John¹,Lee Susie³,Li Lingjie³,Schwertschkow Aaron⁵,Bauer Gerhard⁵,Lisowski Leszek⁶,Kay Mark A.⁶,Kim Seung K.⁴,Lane Alfred T.³,Wernig Marius¹,Oro Anthony E.³

Affiliation:

1. Institute for Stem Cell Biology and Regenerative Medicine, and Department of Pathology, Stanford University, Stanford, CA 94305, USA.

2. Department of Obstetrics and Gynecology, Stanford University, Stanford, CA 94305, USA.

3. Program in Epithelial Biology, Department of Dermatology, Stanford University, Stanford, CA 94305, USA.

4. Department of Developmental Biology, Stanford University, Stanford, CA 94305, USA.

5. Institute for Regenerative Cures, School of Medicine, University of California, Davis, Sacramento, CA 95817, USA.

6. Departments of Pediatrics and Genetics, Stanford University, Stanford, CA 94305, USA.

Abstract

Patient-specific iPSCs were derived, corrected, and differentiated into human skin grafts for the treatment of recessive dystrophic epidermolysis bullosa.

Publisher

American Association for the Advancement of Science (AAAS)

Subject

General Medicine

Reference39 articles.

1. Inherited epidermolysis bullosa: Updated recommendations on diagnosis and classification

2. Epidermolysis Bullosa Care in the United States

3. J. D. Fine L. B. Johnson C. Suchindran E. A. Bauer M. Carter J. McGuire A. Moshell in Epidermolysis Bullosa. Clinical Epidemiologic and Laboratory Advances and the Findings of the National Epidermolysis Bullosa Registry J. D. Fine E. A. Bauer J. McGuire A. Moshell Eds. (The Johns Hopkins University Press Baltimore MD 1999) pp. 175–192.

4. Restoration of type VII collagen expression and function in dystrophic epidermolysis bullosa

5. A Microinjected COL7A1-PAC Vector Restores Synthesis of Intact Procollagen VII in a Dystrophic Epidermolysis Bullosa Keratinocyte Cell Line

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