Long-term correction of ornithine transcarbamylase deficiency in Spf-Ash mice with a translationally optimized AAV vector-Reference-Cited by-同舟云学术

Long-term correction of ornithine transcarbamylase deficiency in Spf-Ash mice with a translationally optimized AAV vector

Published:2021-03 Issue: Volume:20 Page:169-180
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

De Sabbata Giulia,Boisgerault Florence,Guarnaccia Corrado,Iaconcig Alessandra,Bortolussi Giulia,Collaud Fanny,Ronzitti Giuseppe,Sola Marcelo Simon,Vidal Patrice,Rouillon Jeremy,Charles Severine,Nicastro Emanuele,D’Antiga Lorenzo,Ilyinskii Petr,Mingozzi Federico,Kishimoto Takashi Kei,Muro Andrés F.^ORCID

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference55 articles.

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