Lipid nanoparticle-targeted mRNA formulation as a treatment for ornithine-transcarbamylase deficiency model mice
Author:
Funder
Japan Agency for Medical Research and Development
Publisher
Elsevier BV
Subject
Drug Discovery,Molecular Medicine
Reference60 articles.
1. Genetic variation in the urea cycle: a model resource for investigating key candidate genes for common diseases;Mitchell;Hum. Mutat.,2009
2. Urea cycle disorders;Burton;Clin. Liver Dis.,2000
3. Hyperammonemia in pediatric clinics: a review of ornithine transcarbamylase deficiency (OTCD) based on our case studies;Matsuda;JMAJ,2004
4. Genotype-phenotype correlations in ornithine transcarbamylase deficiency: a mutation update;Caldovic;J. Genet. Genomics,2015
5. Genotype spectrum of ornithine transcarbamylase deficiency: correlation with the clinical and biochemical phenotype;McCullough;Am. J. Med. Genet.,2000
Cited by 6 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献
1. The immunostimulatory nature of mRNA lipid nanoparticles;Advanced Drug Delivery Reviews;2024-02
2. Lymph node macrophages drive innate immune responses to enhance the anti-tumor efficacy of mRNA vaccines;Molecular Therapy;2024-01
3. Liver‐directed gene therapy for inherited metabolic diseases;Journal of Inherited Metabolic Disease;2024-01
4. 3D Printing of Dietary Products for the Management of Inborn Errors of Intermediary Metabolism in Pediatric Populations;Nutrients;2023-12-25
5. Delivery of nucleic acids using nanomaterials;Molecular Biomedicine;2023-12-14
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3