Author:
Iyer V Rajesh,Praveen P,Kaduskar Bhagyashree D,Moharir Shivranjani C,Mishra Rakesh K
Publisher
Springer Science and Business Media LLC
Reference222 articles.
1. Akinc A, Maier MA, Manoharan M, et al. 2019 The Onpattro story and the clinical translation of nanomedicines containing nucleic acid-based drugs. Nat. Nanotechnol. 14 1084–1087
2. Al Hafid N and Christodoulou J 2015 Phenylketonuria: a review of current and future treatments. Transl. Pediatr. 4 304–317
3. Alton EWFW AD, Ashby D, et al. on behalf of the UK Cystic Fibrosis Gene Therapy Consortium 2016 A randomised, double-blind, placebo-controlled trial of repeated nebulisation of non-viral cystic fibrosis transmembrane conductance regulator (CFTR) gene therapy in patients with cystic fibrosis (https://www.ncbi.nlm.nih.gov/books/NBK373648/)
4. An D, Schneller JL, Frassetto A, et al. 2017 Systemic messenger RNA therapy as a treatment for methylmalonic acidemia. Cell Rep. 21 3548–3558
5. An D, Frassetto A, Jacquinet E, Eybye M, et al. 2019 Long-term efficacy and safety of mRNA therapy in two murine models of methylmalonic acidemia. eBioMedicine 45 519–528
Cited by
1 articles.
订阅此论文施引文献
订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献