Non-genotoxic conditioning facilitates hematopoietic stem cell gene therapy for hemophilia A using bioengineered factor VIII-Reference-Cited by-同舟云学术

Non-genotoxic conditioning facilitates hematopoietic stem cell gene therapy for hemophilia A using bioengineered factor VIII

Published:2021-06 Issue: Volume:21 Page:710-727
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Russell Athena L.,Prince Chengyu,Lundgren Taran S.,Knight Kristopher A.,Denning Gabriela,Alexander Jordan S.,Zoine Jaquelyn T.,Spencer H. Trent,Chandrakasan Shanmuganathan,Doering Christopher B.

Funder

National Cancer Institute

Winship Cancer Institute

National Institutes of Health

Hemophilia of Georgia

Children's Healthcare of Atlanta

National Heart, Lung, and Blood Institute

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference82 articles.

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4. Replacing bad (F)actors: hemophilia;Doering;Hematology (Am. Soc. Hematol. Educ. Program),2014

5. Advancements in gene transfer-based therapy for hemophilia A;Doering;Expert Rev. Hematol.,2009

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