Efficient Ex Vivo Engineering and Expansion of Highly Purified Human Hematopoietic Stem and Progenitor Cell Populations for Gene Therapy-Reference-Cited by-同舟云学术

Efficient Ex Vivo Engineering and Expansion of Highly Purified Human Hematopoietic Stem and Progenitor Cell Populations for Gene Therapy

Published:2017-04 Issue:4 Volume:8 Page:977-990
ISSN:2213-6711
Container-title:Stem Cell Reports
language:en
Short-container-title:Stem Cell Reports

Author:

Zonari Erika,Desantis Giacomo,Petrillo Carolina,Boccalatte Francesco E.,Lidonnici Maria Rosa,Kajaste-Rudnitski Anna,Aiuti Alessandro,Ferrari Giuliana,Naldini Luigi,Gentner Bernhard

Funder

Telethon Foundation

Telethon-GSK Alliance

Italian Ministry of Health

European Hematology Association

Publisher

Elsevier BV

Subject

Cell Biology,Developmental Biology,Genetics,Biochemistry

Reference37 articles.

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3. In vivo tracking of human hematopoiesis reveals patterns of clonal dynamics during early and steady-state reconstitution phases;Biasco;Cell Stem Cell,2015

4. Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy;Biffi;Science,2013

5. Aryl hydrocarbon receptor antagonists promote the expansion of human hematopoietic stem cells;Boitano;Science,2010

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