Changing respiratory expectations with the new disease trajectory of nusinersen treated spinal muscular atrophy [SMA] type 1
Author:
Publisher
Elsevier BV
Subject
Pulmonary and Respiratory Medicine,Pediatrics, Perinatology and Child Health
Reference66 articles.
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3. Spinal muscular atrophy: diagnosis and management in a new therapeutic era;Arnold;Muscle Nerve,2015
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