Patterns of disease progression in type 2 and 3 SMA: Implications for clinical trials-Reference-Cited by-同舟云学术

Patterns of disease progression in type 2 and 3 SMA: Implications for clinical trials

Published:2016-02 Issue:2 Volume:26 Page:126-131
ISSN:0960-8966
Container-title:Neuromuscular Disorders
language:en
Short-container-title:Neuromuscular Disorders

Author:

Mercuri Eugenio,Finkel Richard,Montes Jacqueline,Mazzone Elena S.,Sormani Maria Pia,Main Marion,Ramsey Danielle,Mayhew Anna,Glanzman Allan M.,Dunaway Sally,Salazar Rachel,Pasternak Amy,Quigley Janet,Pane Marika,Pera Maria Carmela,Scoto Mariacristina,Messina Sonia,Sframeli Maria,Vita Gian Luca,D'Amico Adele,van den Hauwe Marleen,Sivo Serena,Goemans Nathalie,Kaufmann Petra,Darras Basil T.,Bertini Enrico,Muntoni Francesco,De Vivo Darryl C.

Funder

SMA Foundation

SMA Europe

SMA Trust

Famiglie SMA and Telethon

Publisher

Elsevier BV

Subject

Genetics(clinical),Clinical Neurology,Neurology,Pediatrics, Perinatology, and Child Health

Reference21 articles.

1. SMA-EUROPE workshop report: opportunities and challenges in developing clinical trials for spinal muscular atrophy in Europe;Kayadjanian;Orphanet J Rare Dis,2013

2. Childhood spinal muscular atrophy: controversies and challenges;Mercuri;Lancet Neurol,2012