A follow-up study of MPS I patients treated with laronidase enzyme replacement therapy for 6 years-Reference-Cited by-同舟云学术

A follow-up study of MPS I patients treated with laronidase enzyme replacement therapy for 6 years

Published:2007-02 Issue:2 Volume:90 Page:171-180
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Sifuentes Monica,Doroshow Robin,Hoft Richard,Mason Greg,Walot Irwin,Diament Michael,Okazaki Susan,Huff Kenneth,Cox Gerald F.,Swiedler Stuart J.,Kakkis Emil D.

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference15 articles.

1. The Mucopolysaccharidoses;Neufeld,2001

2. The first 5 years of clinical experience with laronidase enzyme replacement therapy for mucopolysaccharidosis I;Wraith;Expert Opin. Pharmacother.,2005

3. The eye as a window to inborn errors of metabolism;Poll-The;J. Inherit. Metab. Dis.,2003

4. Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double-blinded, placebo-controlled, multinational study of recombinant human alpha-l-iduronidase (laronidase);Wraith;J. Pediatr.,2004

5. Enzyme replacement therapy in mucopolysaccharidosis I;Kakkis;N. Engl. J. Med.,2001

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