Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double-blinded, placebo-controlled, multinational study of recombinant human α-L-iduronidase (laronidase)-Reference-Cited by-同舟云学术

Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double-blinded, placebo-controlled, multinational study of recombinant human α-L-iduronidase (laronidase)

Published:2004-05 Issue:5 Volume:144 Page:581-588
ISSN:0022-3476
Container-title:The Journal of Pediatrics
language:en
Short-container-title:The Journal of Pediatrics

Author:

Wraith James E,Clarke Lorne A,Beck Michael,Kolodny Edwin H,Pastores Gregory M,Muenzer Joseph,Rapoport David M,Berger Kenneth I,Swiedler Stuart J,Kakkis Emil D,Braakman Tanja,Chadbourne Elenie,Walton-Bowen Karen,Cox Gerald F

Publisher

Elsevier BV

Subject

Pediatrics, Perinatology and Child Health

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4. Follow-up of nine patients with Hurler syndrome after bone marrow transplantation;Guffon;J Pediatr,1998

5. Hurler syndrome,;Peters;Blood,1998

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