Follow-up of nine patients with Hurler syndrome after bone marrow transplantation
Author:
Publisher
Elsevier BV
Subject
Pediatrics, Perinatology, and Child Health
Reference27 articles.
1. Reversal of clinical features of Hürler’s disease and biochemical improvement after treatment by bone marrow transplantation;Hobbs;Lancet,1981
2. Lysosomal and peroxysomal storage diseases;Harris,1996
3. Outcome of unrelated donor bone marrow transplantation in 40 children with Hurler syndrome;Peters;Blood,1996
4. Long-term outcome of Hürler syndrome following bone marrow transplantation;Whitley;Am J Med Genet,1993
5. Neuropsychological outcomes of several storage diseases with and without bone marrow transplantation;Shapiro;J Inher Metab Dis,1995
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