Long-term correction of hemophilia B using adenoviral delivery of CRISPR/Cas9
Author:
Funder
NIH
NCI Cancer Center
Publisher
Elsevier BV
Subject
Pharmaceutical Science
Reference78 articles.
1. Gene therapy with adeno-associated virus vector 5-human factor IX in adults with hemophilia B;Miesbach;Blood,2017
2. Hemophilia B gene therapy with a high-specific-activity factor IX variant;George;N. Engl. J. Med.,2017
3. Long-term safety and efficacy of factor IX gene therapy in hemophilia B;Nathwani;N. Engl. J. Med.,2014
4. Hepatic gene transfer in neonatal mice by adeno-associated virus serotype 8 vector;Wang;Hum. Gene Ther.,2011
5. Gene delivery to the juvenile mouse liver using rAAV2/8 vectors;Cunningham;Mol. Ther.,2008
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