Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant-Reference-Cited by-同舟云学术

Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant

Published:2017-12-07 Issue:23 Volume:377 Page:2215-2227
ISSN:0028-4793
Container-title:New England Journal of Medicine
language:en
Short-container-title:N Engl J Med

Author:

George Lindsey A.,Sullivan Spencer K.,Giermasz Adam,Rasko John E.J.,Samelson-Jones Benjamin J.,Ducore Jonathan,Cuker Adam,Sullivan Lisa M.,Majumdar Suvankar,Teitel Jerome,McGuinn Catherine E.,Ragni Margaret V.,Luk Alvin Y.,Hui Daniel,Wright J. Fraser,Chen Yifeng,Liu Yun,Wachtel Katie,Winters Angela,Tiefenbacher Stefan,Arruda Valder R.,van der Loo Johannes C.M.,Zelenaia Olga,Takefman Daniel,Carr Marcus E.,Couto Linda B.,Anguela Xavier M.,High Katherine A.

Publisher

Massachusetts Medical Society

Subject

General Medicine

Link

http://www.nejm.org/doi/pdf/10.1056/NEJMoa1708538

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