Hepatic Gene Transfer in Neonatal Mice by Adeno-Associated Virus Serotype 8 Vector-Reference-Cited by-同舟云学术

Hepatic Gene Transfer in Neonatal Mice by Adeno-Associated Virus Serotype 8 Vector

Published:2012-05 Issue:5 Volume:23 Page:533-539
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Wang Lili¹,Wang Huan¹²,Bell Peter¹,McMenamin Deirdre¹,Wilson James M.¹

Affiliation:

1. Gene Therapy Program, and Division of Transfusion Medicine, Department of Pathology and Laboratory Medicine, University of Pennsylvania, Philadelphia, PA 19104.

2. Vaccine Research Institute, Third Affiliated Hospital, Sun Yat-Sen University, 510630 Guangzhou, China.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2011.183

Reference33 articles.

1. Analysis of Tumors Arising in Male B6C3F1 Mice with and without AAV Vector Delivery to Liver

2. Worldwide Epidemiology of Neutralizing Antibodies to Adeno‐Associated Viruses

3. In Vivo Transduction by Intravenous Injection of a Lentiviral Vector Expressing Human ADA into Neonatal ADA Gene Knockout Mice: A Novel Form of Enzyme Replacement Therapy for ADA Deficiency

4. Liver-Directed Recombinant Adeno-Associated Viral Gene Delivery Rescues a Lethal Mouse Model of Methylmalonic Acidemia and Provides Long-Term Phenotypic Correction

5. Long-term Rescue of a Lethal Murine Model of Methylmalonic Acidemia Using Adeno associated Viral Gene Therapy

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