A Tale of Two SCIDs-Reference-Cited by-同舟云学术

A Tale of Two SCIDs

Published:2011-08-24 Issue:97 Volume:3 Page:
ISSN:1946-6234
Container-title:Science Translational Medicine
language:en
Short-container-title:Sci. Transl. Med.

Author:

Shaw Kit L.¹,Kohn Donald B.¹

Affiliation:

1. Department of Microbiology, Immunology and Molecular Genetics and Department of Pediatrics, University of California, Los Angeles, Los Angeles, CA 90095, USA

Abstract

Gene therapy for severe combined immunodeficiency: Do the benefits outweigh the risks?

Publisher

American Association for the Advancement of Science (AAAS)

Subject

General Medicine

Reference28 articles.

1. Long-Term Persistence of a Polyclonal T Cell Repertoire After Gene Therapy for X-Linked Severe Combined Immunodeficiency

2. Hematopoietic Stem Cell Gene Therapy for Adenosine Deaminase–Deficient Severe Combined Immunodeficiency Leads to Long-Term Immunological Recovery and Metabolic Correction

3. Cloning of cDNA sequences of human adenosine deaminase.

4. ADENOSINE-DEAMINASE DEFICIENCY IN TWO PATIENTS WITH SEVERELY IMPAIRED CELLULAR IMMUNITY

5. T Lymphocyte-Directed Gene Therapy for ADA − SCID: Initial Trial Results After 4 Years

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