T Lymphocyte-Directed Gene Therapy for ADA − SCID: Initial Trial Results After 4 Years

Author:

Blaese R. Michael1,Culver Kenneth W.2,Miller A. Dusty3,Carter Charles S.4,Fleisher Thomas4,Clerici Mario2,Shearer Gene2,Chang Lauren5,Chiang Yawen6,Tolstoshev Paul6,Greenblatt Jay J.2,Rosenberg Steven A.2,Klein Harvey4,Berger Melvin7,Mullen Craig A.1,Ramsey W. Jay1,Muul Linda8,Morgan Richard A.9,Anderson W. French5

Affiliation:

1. R. M. Blaese, C. A. Mullen, W. J. Ramsey, National Center for Human Genome Research, National Institutes of Health (NIH), Building 49, Room 2A03, Bethesda, MD 20892, USA, and National Cancer Institute (NCI), NIH, Bethesda, MD 20892, USA.

2. K. W. Culver, M. Clerici, G. Shearer, J. J. Greenblatt, S. A. Rosenberg, NCI, NIH, Bethesda, MD 20892, USA.

3. A. D. Miller, Fred Hutchinson Cancer Research Center, Seattle, WA 98104, USA.

4. C. S. Carter, T. Fleisher, H. Klein, Clinical Center, NIH, Bethesda, MD 20892, USA.

5. L. Chang and W. F. Anderson, National Heart, Lung, and Blood Institute (NHLBI), NIH, Bethesda, MD 20892, USA.

6. Y. Chiang and P. Tolstoshev, Genetic Therapy, Gaithersburg, MD 20878, USA.

7. M. Berger, Department of Pediatrics, Case Western Reserve University School of Medicine, Cleveland, OH 44106, USA.

8. L. Muul, National Center for Human Genome Research, NIH, Bethesda, MD 20892, USA.

9. R. A. Morgan, National Center for Human Genome Research, NIH, Bethesda, MD 20892, USA, and NHLBI, NIH, Bethesda, MD 20892, USA.

Publisher

American Association for the Advancement of Science (AAAS)

Subject

Multidisciplinary

Reference75 articles.

1. NORMAL AND MUTANT HUMAN ADENOSINE-DEAMINASE GENES;AKESON A.L.;JOURNAL OF CELLULAR BIOCHEMISTRY,1989

2. EFFECT OF INTERNAL VIRAL SEQUENCES ON THE UTILITY OF RETROVIRAL VECTORS;ARMENTANO D;JOURNAL OF VIROLOGY,1987

3. SELF DETERMINANTS RECOGNIZED BY HUMAN-VIRUS IMMUNE T-CELLS CAN BE DISTINGUISHED FROM THE SEROLOGICALLY DEFINED HLA ANTIGENS;BIDDISON W.E.;JOURNAL OF IMMUNOLOGY,1980

4. BLAESE R.M., HUM GENE THER 1, 327 (1990).

5. BLAESE R.M., PEDIATR RES: S49 (1993).

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