Biochemical evidence for superior correction of neuronal storage by chemically modified enzyme in murine mucopolysaccharidosis VII
Author:
Publisher
Proceedings of the National Academy of Sciences
Subject
Multidisciplinary
Reference52 articles.
1. Beta glucuronidase deficiency: Report of clinical, radiologic, and biochemical features of a new mucopolysaccharidosis
2. Enzyme replacement therapy for Gaucher disease
3. Globotriaosylceramide accumulation in the Fabry kidney is cleared from multiple cell types after enzyme replacement therapy
4. A Phase 1/2 Clinical Trial of Enzyme Replacement in Fabry Disease: Pharmacokinetic, Substrate Clearance, and Safety Studies
5. Long-Term Safety and Efficacy of Enzyme Replacement Therapyfor Fabry Disease
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