Publisher
Public Library of Science (PLoS)
Reference33 articles.
1. Regulation (EC) No 141/2000 of the European Parliament and of the Council of 16 December 1999 on orphan medicinal products;Off J Eur Communities,2000
2. Council recommendation of 8 June 2009 on an action in the field of rare diseases;Off J Eur Union,2009
3. Recommendations for the development of rare disease drugs using the accelerated approval pathway and for qualifying biomarkers as primary endpoints;ED Kakkis;Orphanet J Rare Dis,2015
4. Clinical trials of orphan medicines;BM Buckley;Lancet,2008
5. Clinical research for rare disease: opportunities, challenges, and solutions;RC Griggs;Mol Genet Metab,2009
Cited by
21 articles.
订阅此论文施引文献
订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献