Clinical research for rare disease: Opportunities, challenges, and solutions-Reference-Cited by-同舟云学术

Clinical research for rare disease: Opportunities, challenges, and solutions

Published:2009-01 Issue:1 Volume:96 Page:20-26
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Griggs Robert C.,Batshaw Mark,Dunkle Mary,Gopal-Srivastava Rashmi,Kaye Edward,Krischer Jeffrey,Nguyen Tan,Paulus Kathleen,Merkel Peter A.

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference28 articles.

1. Orphan Drug Act, Pub. L. No 97-414, 96 Stat. 2049 (1984 as amended).

2. Available from: .

3. The tax provisions are administered by the Internal Revenue Service (see Title 26, Code of Federal Regulations, Section 45C)—Dr. Nguyen—OK?

4. See Title 21, Code of Federal Regulations, Part 316.

5. J. Mitsumoto, E.R. Dorsey, J. Thompson, R.C. Griggs, Impact of the Orphan Drug Act on Drug Development. Presented at the Conference on Clinical Research for Rare Diseases, September 5, 2007, Bethesda, MD.

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