SuccessfulRPE65Gene Replacement and Improved Visual Function in Humans
Author:
Publisher
Informa UK Limited
Subject
Genetics (clinical),Ophthalmology,Pediatrics, Perinatology and Child Health
Link
http://www.tandfonline.com/doi/pdf/10.1080/13816810802216480
Reference15 articles.
1. An overview of leber congenital amaurosis: a model to understand human retinal development
2. Functional and Structural Evaluation after AAV.RPE65 Gene Transfer in the Canine Model of Leber’s Congenital Amaurosis
3. Molecular cloning and expression of RPE65, a novel retinal pigment epithelium-specific microsomal protein that is post-transcriptionally regulated in vitro
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