CRISPR-Cas9 correction of a nonsense mutation in LCA5 rescues lebercilin expression and localization in human retinal organoids-Reference-Cited by-同舟云学术

CRISPR-Cas9 correction of a nonsense mutation in LCA5 rescues lebercilin expression and localization in human retinal organoids

Published:2023-06 Issue: Volume:29 Page:522-531
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Afanasyeva Tess A.V.,Athanasiou Dimitra,Perdigao Pedro R.L.,Whiting Kae R.,Duijkers Lonneke,Astuti Galuh D.N.,Bennett Jean,Garanto Alejandro,van der Spuy Jacqueline,Roepman Ronald,Cheetham Michael E.,Collin Rob W.J.^ORCID

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

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