Protease-resistant modified human β-hexosaminidase B ameliorates symptoms in GM2 gangliosidosis model-Reference-Cited by-同舟云学术

Protease-resistant modified human β-hexosaminidase B ameliorates symptoms in GM2 gangliosidosis model

Published:2016-03-28 Issue:5 Volume:126 Page:1691-1703
ISSN:0021-9738
Container-title:Journal of Clinical Investigation
language:en
Short-container-title:

Author:

Kitakaze Keisuke,Mizutani Yasumichi,Sugiyama Eiji,Tasaki Chikako,Tsuji Daisuke,Maita Nobuo,Hirokawa Takatsugu,Asanuma Daisuke,Kamiya Mako,Sato Kohei,Setou Mitsutoshi,Urano Yasuteru,Togawa Tadayasu,Otaka Akira,Sakuraba Hitoshi,Itoh Kohji

Publisher

American Society for Clinical Investigation

Subject

General Medicine

Reference61 articles.

1. Reversibility of neuropathology in Tay–Sachs-related diseases

2. Therapeutic Response in Feline Sandhoff Disease Despite Immunity to Intracranial Gene Therapy

3. Highly phosphomannosylated enzyme replacement therapy for GM2 gangliosidosis

4. Therapeutic Potential of Intracerebroventricular Replacement of Modified Human β-Hexosaminidase B for GM2 Gangliosidosis

Cited by 26 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Treating late-onset Tay Sachs disease: Brain delivery with a dual trojan horse protein;Molecular Therapy - Methods & Clinical Development;2024-09

2. Innate immune sensing of lysosomal dysfunction drives multiple lysosomal storage disorders;Nature Cell Biology;2024-01-22

3. Lysoglycosphingolipids have the ability to induce cell death through direct PI3K inhibition;Journal of Neurochemistry;2023-11-17

4. α-Mannosidase and β-d-N-acetylhexosaminidase outside the wall: partner exoglycosidases involved in fruit ripening process;Plant Molecular Biology;2023-05-13

5. Pathophysiology of Sandhoff Disease and Novel Thrapeutic Targets;YAKUGAKU ZASSHI;2023-01-01