Sustained Human Factor VIII Expression in Hemophilia A Mice Following Systemic Delivery of a Gutless Adenoviral Vector-Reference-Cited by-同舟云学术

Sustained Human Factor VIII Expression in Hemophilia A Mice Following Systemic Delivery of a Gutless Adenoviral Vector

Published:2002-01 Issue:1 Volume:5 Page:63-73
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Reddy P.Seshidhar,Sakhuja Kiran,Ganesh Shanthi,Yang Lijuan,Kayda Dawn,Brann Terrence,Pattison Scott,Golightly Doug,Idamakanti Neeraja,Pinkstaff Anne,Kaloss Michele,Barjot Catherine,Chamberlain Jeffrey S.,Kaleko Michael,Connelly Sheila

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference49 articles.

1. High-level tissue-specific expression of functional human factor VIII in mice;Connelly;Hum. Gene Ther.,1996

2. Sustained phenotypic correction of murine hemophilia A by in vivo gene therapy;Connelly;Blood,1998

3. In vivo evaluation of an adenoviral vectorecoding canine factor VIII: high-level, sustained expression in hemophiliac mice;Gallo-Penn;Hum. Gene Ther.,1999

4. Complete short-term correction of canine hemophilia A by in vivo gene therapy;Connelly;Blood,1996

5. Systemic delivery of an adenoviral vector encoding canine factor VIII results in short-term phenotypic correction, inhibitor development, and biphasic liver toxicity in hemophilia A dogs;Gallo-Penn;Blood,2001

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