Intramuscular Administration of Recombinant Adeno-Associated Virus 2 α-1 Antitrypsin (rAAV-SERPINA1) Vectors in a Nonhuman Primate Model: Safety and Immunologic Aspects-Reference-Cited by-同舟云学术

Intramuscular Administration of Recombinant Adeno-Associated Virus 2 α-1 Antitrypsin (rAAV-SERPINA1) Vectors in a Nonhuman Primate Model: Safety and Immunologic Aspects

Published:2002-09 Issue:3 Volume:6 Page:329-335
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Song Sihong,Scott-Jorgensen Marda,Wang Jianming,Poirier Amy,Crawford James,Campbell-Thompson Martha,Flotte Terence R.

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference18 articles.

1. Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein;Kessler;Proc. Natl. Acad. Sci. USA,1996

2. Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors;Snyder;Nat. Genet.,1997

3. Sustained secretion of human α-1-antitrypsin from murine muscle transduced with adeno-associated virus vectors;Song;Proc. Natl. Acad. Sci. USA,1998

4. Stable therapeutic serum levels of human α-1 antitrypsin (AAT) after portal vein injection of recombinant adeno-associated virus (rAAV) vectors;Song;Gene Ther.,2001

5. Long-term correction of obesity and diabetes in genetically obese mice by a single intramuscular injection of recombinant adeno-associated virus encoding mouse leptin;Murphy;Proc. Natl. Acad. Sci. USA,1997

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