Stable therapeutic serum levels of human alpha-1 antitrypsin (AAT) after portal vein injection of recombinant adeno-associated virus (rAAV) vectors-Reference-Cited by-同舟云学术

Stable therapeutic serum levels of human alpha-1 antitrypsin (AAT) after portal vein injection of recombinant adeno-associated virus (rAAV) vectors

Published:2001-09 Issue:17 Volume:8 Page:1299-1306
ISSN:0969-7128
Container-title:Gene Therapy
language:en
Short-container-title:Gene Ther

Author:

Song S,Embury J,Laipis PJ,Berns KI,Crawford JM,Flotte TR

Publisher

Springer Science and Business Media LLC

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.nature.com/articles/3301422.pdf

Reference33 articles.

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3. Sharp HL, Bridges RA, Krivit W, Freier EF . Cirrhosis associated with alpha-1-antitrypsin deficiency: a previously unrecognized inherited disorder J Lab Clin Med 1969 73: 934–939

4. Lomas DA, Evans DL, Finch JT, Carrell RW . The mechanism of Z alpha 1-antitrypsin accumulation in the liver (see comments) Nature 1992 357: 605–607

5. Lomas DA . Loop-sheet polymerization: the mechanism of alpha1-antitrypsin deficiency Respir Med 2000 94: (Suppl. C) S3–6

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