Antisense oligonucleotides correct the familial dysautonomia splicing defect in IKBKAP transgenic mice-Reference-Cited by-同舟云学术

Antisense oligonucleotides correct the familial dysautonomia splicing defect in IKBKAP transgenic mice

Author:

Sinha Rahul¹²,Kim Young Jin¹³,Nomakuchi Tomoki¹³,Sahashi Kentaro¹⁴,Hua Yimin¹⁵,Rigo Frank⁶,Bennett C Frank⁶,Krainer Adrian R¹

Affiliation:

1. Cold Spring Harbor Laboratory, Cold Spring Harbor, NY 11724, USA

2. Institute for Stem Cell Biology and Regenerative Medicine, Stanford University School of Medicine, Stanford, CA 94305, USA

3. Stony Brook University School of Medicine, Stony Brook, NY 11790, USA

4. Department of Neurology, Nagoya University Graduate School of Medicine, Nagoya 466-8550, Japan

5. Institute of Neuroscience, Soochow University, Suzhou, Jiangsu 215123, China

6. Ionis Pharmaceuticals, Carlsbad, CA 92008, USA

Funder

National Institutes of Health

Publisher

Oxford University Press (OUP)

Subject

Genetics

Link

Reference43 articles.

1. Familial dysautonomia;Slaugenhaupt;Curr. Opin. Genet. Dev.,2002

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