Micro-dystrophin and follistatin co-delivery restores muscle function in aged DMD model-Reference-Cited by-同舟云学术

Micro-dystrophin and follistatin co-delivery restores muscle function in aged DMD model

Published:2013-07-17 Issue:24 Volume:22 Page:4929-4937
ISSN:1460-2083
Container-title:Human Molecular Genetics
language:en
Short-container-title:

Author:

Rodino-Klapac Louise R.,Janssen Paul M. L.,Shontz Kimberly M.,Canan Benjamin,Montgomery Chrystal L.,Griffin Danielle,Heller Kristin,Schmelzer Leah,Handy Chalonda,Clark K. Reed,Sahenk Zarife,Mendell Jerry R.,Kaspar Brian K.

Publisher

Oxford University Press (OUP)

Subject

Genetics(clinical),Genetics,Molecular Biology,General Medicine

Link

http://academic.oup.com/hmg/article-pdf/22/24/4929/14139985/ddt342.pdf

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4. AAV vector-mediated microdystrophin expression in a relatively small percentage of mdx myofibers improved the mdx phenotype;Yoshimura;Mol. Ther.,2004

5. A translational approach for limb vascular delivery of the micro-dystrophin gene without high volume or high pressure for treatment of Duchenne muscular dystrophy;Rodino-Klapac;J. Transl. Med.,2007

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