Dual FKRP/FST gene therapy normalizes ambulation, increases strength, decreases pathology, and amplifies gene expression in LGMDR9 mice
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Published:2024-08
Issue:8
Volume:32
Page:2604-2623
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ISSN:1525-0016
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Container-title:Molecular Therapy
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language:en
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Short-container-title:Molecular Therapy
Author:
Lam Patricia,
Zygmunt Deborah A.,
Ashbrook Anna,
Bennett Macey,
Vetter Tatyana A.,
Martin Paul T.ORCID
Funder
LGMD2I Research Fund