Enhanced Response to Enzyme Replacement Therapy in Pompe Disease after the Induction of Immune Tolerance
Author:
Publisher
Elsevier BV
Subject
Genetics (clinical),Genetics
Reference39 articles.
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3. Clinical and metabolic correction of Pompe disease by enzyme therapy in acid maltase-deficient quail;Kikuchi;J Clin Invest,1998
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5. Enzyme replacement therapy in the mouse model of Pompe disease;Raben;Mol Genet Metab,2003
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