Phase I study of liver depot gene therapy in late-onset Pompe disease-Reference-Cited by-同舟云学术

Phase I study of liver depot gene therapy in late-onset Pompe disease

Published:2023-07 Issue:7 Volume:31 Page:1994-2004
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Smith Edward C.,Hopkins Sam,Case Laura E.,Xu Ming,Walters Crista,Dearmey Stephanie,Han Sang-oh,Spears Tracy G.,Chichester Jessica A.,Bossen Edward H.,Hornik Christoph P.,Cohen Jennifer L.,Bali Deeksha,Kishnani Priya S.,Koeberl Dwight D.^ORCID

Funder

NIAMS

NCATS

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference56 articles.

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