Adjunctive β 2 ‐agonist treatment reduces glycogen independently of receptor‐mediated acid α‐glucosidase uptake in the limb muscles of mice with Pompe disease-Reference-Cited by-同舟云学术

Adjunctive β 2 ‐agonist treatment reduces glycogen independently of receptor‐mediated acid α‐glucosidase uptake in the limb muscles of mice with Pompe disease

Published:2014-01-21 Issue:5 Volume:28 Page:2272-2280
ISSN:0892-6638
Container-title:The FASEB Journal
language:en
Short-container-title:FASEB j.

Author:

Farah Benjamin L.¹,Madden Lauran²,Li Songtao³,Nance Sierra³,Bird Andrew³,Bursac Nenad²,Yen Paul M.¹⁴⁵⁶,Young Sarah P.³,Koeberl Dwight D.³

Affiliation:

1. Cardiovascular and Metabolic Disease ProgramDuke–National University of Singapore Graduate Medical SchoolSingaporeSingapore

2. Department of Biomedical EngineeringDuke University Medical CenterDurhamNorth CarolinaUSA

3. Division of Medical GeneticsDepartment of PediatricsDuke University Medical CenterDurhamNorth CarolinaUSA

4. Sarah W. Stedman Nutrition and Metabolism CenterDuke University Medical CenterDurhamNorth CarolinaUSA

5. Department of Medicine and PharmacologyDuke University Medical CenterDurhamNorth CarolinaUSA

6. Department of Cancer BiologyDuke University Medical CenterDurhamNorth CarolinaUSA

Funder

National Institutes of Health

National Heart, Lung, and Blood Institute

Naval Medical Research Center

Genzyme

Publisher

Wiley

Subject

Genetics,Molecular Biology,Biochemistry,Biotechnology

Link

https://onlinelibrary.wiley.com/doi/pdf/10.1096/fj.13-244202

Reference38 articles.

1. Enzyme replacement therapy in the mouse model of Pompe disease

2. Enhanced efficacy of enzyme replacement therapy in Pompe disease through mannose-6-phosphate receptor expression in skeletal muscle

3. β2 Agonists enhance the efficacy of simultaneous enzyme replacement therapy in murine Pompe disease

4. Adjunctive β2‐agonists reverse neuromuscular involvement in murine Pompe disease

5. Genetic Fate of Recombinant Adeno-Associated Virus Vector Genomes in Muscle

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