Salmeterol enhances the cardiac response to gene therapy in Pompe disease
Author:
Funder
NIH
Publisher
Elsevier BV
Subject
Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism
Reference26 articles.
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2. Oropharyngeal dysphagia in infants and children with infantile Pompe disease;Jones;Dysphagia,2009
3. Clinical and histologic ocular findings in pompe disease;Yanovitch;J. Pediatr. Ophthalmol. Strabismus,2010
4. Enzyme replacement therapy in the mouse model of Pompe disease;Raben;Mol. Genet. Metab.,2003
5. Replacing acid alpha-glucosidase in Pompe disease: recombinant and transgenic enzymes are equipotent, but neither completely clears glycogen from type II muscle fibers;Raben;Mol. Ther.,2005
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2. Efficacious Androgen Hormone Administration in Combination with Adeno-Associated Virus Vector-Mediated Gene Therapy in Female Mice with Pompe Disease;Human Gene Therapy;2022-05-01
3. What’s new and what’s next for gene therapy in Pompe disease?;Expert Opinion on Biological Therapy;2022-04-27
4. Neuromuscular Development and Disease: Learning From in vitro and in vivo Models;Frontiers in Cell and Developmental Biology;2021-10-27
5. Three-dimensional tissue-engineered human skeletal muscle model of Pompe disease;Communications Biology;2021-05-05
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