Replacing acid α-glucosidase in Pompe disease: recombinant and transgenic enzymes are equipotent, but neither completely clears glycogen from type II muscle fibers-Reference-Cited by-同舟云学术

Replacing acid α-glucosidase in Pompe disease: recombinant and transgenic enzymes are equipotent, but neither completely clears glycogen from type II muscle fibers

Published:2005-01 Issue:1 Volume:11 Page:48-56
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Raben Nina,Fukuda Tokiko,Gilbert Abigail L.,de Jong Deborah,Thurberg Beth L.,Mattaliano Robert J.,Meikle Peter,Hopwood John J.,Nagashima Kunio,Nagaraju Kanneboyina,Plotz Paul H.

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference59 articles.

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