Cell and Gene Therapy for the Beta-Thalassemias: Advances and Prospects
Author:
Affiliation:
1. Center for Cell Engineering, Memorial Sloan Kettering Cancer Center, New York, New York.
2. Department of Pediatrics, Memorial Sloan Kettering Cancer Center, New York, New York.
Publisher
Mary Ann Liebert Inc
Subject
Genetics,Molecular Biology,Molecular Medicine
Link
http://www.liebertpub.com/doi/pdf/10.1089/hum.2016.037
Reference76 articles.
1. StamatoyannopoulosG, NienhuisAW, MajerusP, VarmusH, eds. The Molecular Basis of Blood Diseases. (WB Saunders, Philadelphia, PA). 2001.
2. Therapeutic Options for Patients with Severe β-Thalassemia: The Need for Globin Gene Therapy
3. Improved survival in thalassemia major patients on switching from desferrioxamine to combined chelation therapy with desferrioxamine and deferiprone
4. Survival in a large cohort of Greek patients with transfusion-dependent beta thalassaemia and mortality ratios compared to the general population
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