Therapeutic Options for Patients with Severe β-Thalassemia: The Need for Globin Gene Therapy-Reference-Cited by-同舟云学术

Therapeutic Options for Patients with Severe β-Thalassemia: The Need for Globin Gene Therapy

Published:2007-01 Issue:1 Volume:18 Page:1-9
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Sadelain Michel¹,Boulad Farid²,Galanello Renzo³,Giardina Patricia⁴,Locatelli Franco⁵,Maggio Aurelio⁶,Rivella Stefano⁴,Riviere Isabelle⁷,Tisdale John⁸

Affiliation:

1. Gene Transfer and Gene Expression Laboratory, Department of Medicine and Immunology Program, Memorial Sloan-Kettering Cancer Center, New York, NY 10021.

2. Department of Pediatrics, Memorial Sloan-Kettering Cancer Center, New York, NY 10021.

3. Clinica Pediatrica, Ospedale Regionale Microcitemie, I-09121Cagliari, Italy.

4. Department of Pediatrics, New York-Presbyterian Hospital/Weill Medical College of Cornell University, New York, NY 10021.

5. Oncoematologia Pediatrica, IRCCS Policlinico San Matteo, University of Pavia, I-27100 Pavia, Italy.

6. Division of Hematology II and Piera Cutino Research Unit, Azienda Ospedaliera Vincenzo Cervello, I-90146 Palermo, Italy.

7. Gene Transfer and Somatic Cell Engineering Facility, Department of Medicine and Immunology Program, Memorial Sloan-Kettering Cancer Center, New York, NY 10021.

8. Molecular and Clinical Hematology Branch, National Institute of Diabetes and Digestive and Kidney Diseases, National Institutes of Health, Bethesda, MD 20892.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2006.151

Reference63 articles.

1. Correction of ADA-SCID by Stem Cell Gene Therapy Combined with Nonmyeloablative Conditioning

2. Persistence of mixed chimerism in patients transplanted for the treatment of thalassemia

3. Phlebotomy to Reduce Iron Overload in Patients Cured of Thalassemia by Bone Marrow Transplantation

4. Side effects of retroviral gene transfer into hematopoietic stem cells

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