Triple Trans-Splicing Adeno-Associated Virus Vectors Capable of Transferring the Coding Sequence for Full-Length Dystrophin Protein into Dystrophic Mice-Reference-Cited by-同舟云学术

Triple Trans-Splicing Adeno-Associated Virus Vectors Capable of Transferring the Coding Sequence for Full-Length Dystrophin Protein into Dystrophic Mice

Published:2014-02 Issue:2 Volume:25 Page:98-108
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Koo Taeyoung¹²,Popplewell Linda¹,Athanasopoulos Takis¹³,Dickson George¹

Affiliation:

1. School of Biological Sciences, Royal Holloway University of London, Surrey TW20 0EX, United Kingdom.

2. Department of Physiology, Anatomy and Genetics, University of Oxford, Oxford OX1 3QX, United Kingdom.

3. Faculty of Science and Engineering, University of Wolverhampton, Wolverhampton WV1 1LY, United Kingdom.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2013.164

Reference27 articles.

1. Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice

2. Truncated dystrophins can influence neuromuscular synapse structure

3. Codon and mRNA Sequence Optimization of Microdystrophin Transgenes Improves Expression and Physiological Outcome in Dystrophic mdx Mice Following AAV2/8 Gene Transfer

4. Viral serotype and the transgene sequence influence overlapping adeno-associated viral (AAV) vector-mediated gene transfer in skeletal muscle

5. Systemic Trans-Splicing Adeno-Associated Viral Delivery Efficiently Transduces the Heart of Adult mdx Mouse, a Model for Duchenne Muscular Dystrophy

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