Gene Delivery for Limb-Girdle Muscular Dystrophy Type 2D by Isolated Limb Infusion-Reference-Cited by-同舟云学术

Gene Delivery for Limb-Girdle Muscular Dystrophy Type 2D by Isolated Limb Infusion

Published:2019-07 Issue:7 Volume:30 Page:794-801
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Mendell Jerry R.¹²³,Chicoine Louis G.¹²,Al-Zaidy Samiah A.²,Sahenk Zarife¹²³,Lehman Kelly¹,Lowes Linda¹²³,Miller Natalie¹,Alfano Lindsay¹³,Galliers Beverly¹,Lewis Sarah¹,Murrey Darren¹,Peterson Ellyn¹,Griffin Danielle A.¹,Church Kathleen¹,Cheatham Sharon⁴,Cheatham John⁴,Hogan Mark J.⁵,Rodino-Klapac Louise R.¹²

Affiliation:

1. Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, Ohio.

2. Department of Pediatrics, The Ohio State University, Columbus, Ohio.

3. Department of Neurology, The Ohio State University, Columbus, Ohio.

4. Department of Interventional Cardiology, The Ohio State University, Columbus, Ohio.

5. Department of Radiology, Vascular and Interventional Radiology, Nationwide Children's Hospital, Columbus, Ohio.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2019.006

Reference32 articles.

1. Limb-girdle muscular dystrophy type 2D gene therapy restores α-sarcoglycan and associated proteins

2. Sustained alpha-sarcoglycan gene expression after gene transfer in limb-girdle muscular dystrophy, type 2D

3. Delivery ofα- andβ-Sarcoglycan by Recombinant Adeno-Associated Virus: Efficient Rescue of Muscle, but Differential Toxicity

4. Isolated limb perfusion of soft tissue sarcomas: A comprehensive review of literature

5. A translational approach for limb vascular delivery of the micro-dystrophin gene without high volume or high pressure for treatment of Duchenne muscular dystrophy

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