Delivery ofα- andβ-Sarcoglycan by Recombinant Adeno-Associated Virus: Efficient Rescue of Muscle, but Differential Toxicity-Reference-Cited by-同舟云学术

Delivery ofα- andβ-Sarcoglycan by Recombinant Adeno-Associated Virus: Efficient Rescue of Muscle, but Differential Toxicity

Published:2002-09 Issue:13 Volume:13 Page:1631-1646
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Dressman D.¹,Araishi K.²,Imamura M.²,Sasaoka T.²,Liu L.A.³,Engvall E.³,Hoffman E.P.¹

Affiliation:

1. Research Center for Genetic Medicine, Children's National Medical Center, Washington, D.C. 20010 and Department of Molecular Genetics and Biochemistry, University of Pittsburgh, Pittsburgh, PA 15260

2. National Institute of Neuroscience, National Center of Neurology and Psychiatry, Tokyo 187, Japan

3. Burnham Institute, La Jolla, CA 92037

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/10430340260201725

Reference38 articles.

1. Early adenovirus-mediated gene transfer effectively prevents muscular dystrophy in alpha-sarcoglycan-deficient mice

2. Loss of the Sarcoglycan Complex and Sarcospan Leads to Muscular Dystrophy in -Sarcoglycan-Deficient Mice

3. Adeno-Associated Viruses: An Update

4. The role of receptors in the maturation-dependent adenoviral transduction of myofibers

5. Expression Profiling in the Muscular Dystrophies

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