Intrapleural Administration of an AAVrh.10 Vector Coding for Human α1-Antitrypsin for the Treatment of α1-Antitrypsin Deficiency-Reference-Cited by-同舟云学术

Intrapleural Administration of an AAVrh.10 Vector Coding for Human α1-Antitrypsin for the Treatment of α1-Antitrypsin Deficiency

Published:2013-12 Issue:4 Volume:24 Page:161-173
ISSN:2324-8637
Container-title:Human Gene Therapy Clinical Development
language:en
Short-container-title:Human Gene Therapy Clinical Development

Author:

Chiuchiolo Maria J.¹,Kaminsky Stephen M.¹,Sondhi Dolan¹,Hackett Neil R.¹,Rosenberg Jonathan B.¹,Frenk Esther Z.¹,Hwang Yihharn¹,Van de Graaf Benjamin G.¹,Hutt Julie A.²,Wang Gensheng²,Benson Janet²,Crystal Ronald G.¹

Affiliation:

1. Department of Genetic Medicine, Weill Cornell Medical College, New York, NY 10065.

2. Lovelace Respiratory Research Institute, Albuquerque, NM 87108-5127.

Publisher

Mary Ann Liebert Inc

Subject

Genetics (clinical)

Link

http://www.liebertpub.com/doi/pdf/10.1089/humc.2013.168

Reference50 articles.

1. Oxidation of Z α1-Antitrypsin by Cigarette Smoke Induces Polymerization

2. Survival and FEV1Decline in Individuals with Severe Deficiency of α1-Antitrypsin

3. American Thoracic Society/European Respiratory Society Statement

4. Molecular basis of alpha-1-antitrypsin deficiency

5. Clinical Features and History of the Destructive Lung Disease Associated with Alpha-1-Antitrypsin Deficiency of Adults with Pulmonary Symptoms

Cited by 51 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. The longitudinal kinetics of AAV5 vector integration profiles and evaluation of clonal expansion in mice;Molecular Therapy - Methods & Clinical Development;2024-09

2. Prophylactic Prednisolone Promotes AAV5 Hepatocyte Transduction Through the Novel Mechanism of AAV5 Coreceptor Platelet-Derived Growth Factor Receptor Alpha Upregulation and Innate Immune Suppression;Human Gene Therapy;2024-01-01

3. Positron Emission Tomography Quantitative Assessment of Off-Target Whole-Body Biodistribution of I-124-Labeled Adeno-Associated Virus Capsids Administered to Cerebral Spinal Fluid;Human Gene Therapy;2023-10-23

4. Alpha-1 antitrypsin deficiency: current therapy and emerging targets;Expert Review of Respiratory Medicine;2023-03-04

5. Various AAV Serotypes and Their Applications in Gene Therapy: An Overview;Cells;2023-03-01