Prophylactic Prednisolone Promotes AAV5 Hepatocyte Transduction Through the Novel Mechanism of AAV5 Coreceptor Platelet-Derived Growth Factor Receptor Alpha Upregulation and Innate Immune Suppression-Reference-Cited by-同舟云学术

Prophylactic Prednisolone Promotes AAV5 Hepatocyte Transduction Through the Novel Mechanism of AAV5 Coreceptor Platelet-Derived Growth Factor Receptor Alpha Upregulation and Innate Immune Suppression

Published:2024-01-01 Issue:1-2 Volume:35 Page:36-47
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Handyside Britta¹,Zhang Lening¹,Yates Bridget¹,Xie Lin¹,Ismail Ashrafali Mohamed¹^ORCID,Murphy Ryan¹,Baridon Brian¹,Su Cheng²,Bouwman Taren¹,Mangini Linley¹,Tahquechi Jorden¹,Salcido Sandra¹,Minto Wesley C.¹,Keenan William T.¹,Ntai Ioanna³,Sihn Choong-Ryoul¹,Bullens Sherry¹,Bunting Stuart¹,Fong Sylvia¹

Affiliation:

1. Biology Research; BioMarin Pharmaceutical, Inc.; Novato, California, USA.

2. Global Clinical Sciences; BioMarin Pharmaceutical, Inc.; Novato, California, USA.

3. Translational Sciences; BioMarin Pharmaceutical, Inc.; Novato, California, USA.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2023.065

Reference64 articles.

1. Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B

2. Multiyear Factor VIII Expression after AAV Gene Transfer for Hemophilia A

3. Human Immune Responses to Adeno-Associated Virus (AAV) Vectors

4. Long-Term Follow-Up of the First in Human Intravascular Delivery of AAV for Gene Transfer: AAV2-hFIX16 for Severe Hemophilia B

5. Overcoming innate immune barriers that impede AAV gene therapy vectors

Cited by 1 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Enhanced transgene expression from single-stranded AAV vectors in human cells in vitro and in murine hepatocytes in vivo;Molecular Therapy - Nucleic Acids;2024-06