An Improved Adeno-Associated Virus Vector for Neurological Correction of the Mouse Model of Mucopolysaccharidosis IIIA-Reference-Cited by-同舟云学术

An Improved Adeno-Associated Virus Vector for Neurological Correction of the Mouse Model of Mucopolysaccharidosis IIIA

Published:2019-09-01 Issue:9 Volume:30 Page:1052-1066
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Gray Anna L.¹,O'Leary Claire¹,Liao Aiyin¹,Agúndez Leticia²,Youshani Amir S.¹,Gleitz Hélène F.¹,Parker Helen¹,Taylor Jessica T.¹,Danos Olivier³,Hocquemiller Michaël³,Palomar Nuria²,Linden R. Michael²,Henckaerts Els²,Holley Rebecca J.¹,Bigger Brian W.¹

Affiliation:

1. Stem Cell and Neurotherapies, Division of Cell Matrix Biology and Regenerative Medicine, Faculty of Biology, Medicine and Health, The University of Manchester, Manchester, Manchester, United Kingdom

2. Department of Infectious Diseases, School of Immunology and Microbial Sciences, King's College London, London, United Kingdom

3. Lysogene, Neuilly-sur-Seine, France.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2018.189

Reference38 articles.

1. Sanfilippo syndrome: A mini-review

2. Incidence and natural history of mucopolysaccharidosis type III in France and comparison with United Kingdom and Greece

3. Neuropathology in Mouse Models of Mucopolysaccharidosis Type I, IIIA and IIIB