A Novel BaEVRless-Pseudotyped γ-Globin Lentiviral Vector Drives High and Stable Fetal Hemoglobin Expression and Improves Thalassemic ErythropoiesisIn Vitro-Reference-Cited by-同舟云学术

A Novel BaEVRless-Pseudotyped γ-Globin Lentiviral Vector Drives High and Stable Fetal Hemoglobin Expression and Improves Thalassemic ErythropoiesisIn Vitro

Published:2019-05 Issue:5 Volume:30 Page:601-617
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Drakopoulou Ekati¹²,Georgomanoli Maria¹²,Lederer Carsten W.³⁴,Kleanthous Marina³⁴,Costa Caroline⁵,Bernadin Ornellie⁵,Cosset François-Loïc⁵,Voskaridou Ersi⁶,Verhoeyen Els⁵⁷,Papanikolaou Eleni¹²,Anagnou Nicholas P.¹²

Affiliation:

1. Laboratory of Cell and Gene Therapy, Centre for Basic Research, Biomedical Research Foundation of the Academy of Athens (BRFAA), Athens, Greece

2. Laboratory of Biology, University of Athens School of Medicine, Athens, Greece

3. Department of Molecular Genetics Thalassemia, The Cyprus Institute of Neurology and Genetics, Nicosia, Cyprus

4. Cyprus School of Molecular Medicine, Nicosia, Cyprus

5. CIRI—International Center for Infectiology Research, Inserm, U1111, Université Claude Bernard Lyon 1, CNRS, UMR 5308, Ecole Normale Supérieure de Lyon, Lyon, France

6. Thalassemia and Sickle Cell Disease Centre, Laikon General Hospital, Athens, Greece

7. Inserm, U1065, Centre Méditerranéen de Médecine Moléculaire (C3M), Equipe Contrôle Métabolique des Morts Cellulaires, Nice, France

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

https://www.liebertpub.com/doi/pdf/10.1089/hum.2018.022

Reference49 articles.

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