scAAV9 Intracisternal Delivery Results in Efficient Gene Transfer to the Central Nervous System of a Feline Model of Motor Neuron Disease-Reference-Cited by-同舟云学术

scAAV9 Intracisternal Delivery Results in Efficient Gene Transfer to the Central Nervous System of a Feline Model of Motor Neuron Disease

Published:2013-07 Issue:7 Volume:24 Page:670-682
ISSN:1043-0342
Container-title:Human Gene Therapy
language:en
Short-container-title:Human Gene Therapy

Author:

Bucher Thomas¹,Colle Marie-Anne²,Wakeling Erin³,Dubreil Laurence²,Fyfe John³,Briot-Nivard Delphine¹,Maquigneau Maud¹,Raoul Sylvie¹,Cherel Yan²,Astord Stéphanie⁴,Duque Sandra⁴,Marais Thibaut⁴,Voit Thomas⁴,Moullier Philippe¹⁵,Barkats Martine⁴,Joussemet Béatrice¹

Affiliation:

1. INSERM UMR1089, Institut de Recherche Thérapeutique 1, Université de Nantes, 44007 Nantes Cedex 01, France.

2. INRA UMR703, Ecole Nationale Vétérinaire, Agroalimentaire et de l'Alimentation Nantes-Atlantique (Oniris), 44307, Nantes, France.

3. Department of Microbiology and Molecular Genetics, Michigan State University, 2209 Biomedical Physical Sciences, Lansing, Michigan, MI 48824–4320.

4. INSERM UMR974, Institut de Myologie, Faculté de Médecine, 75013 Paris, France.

5. Department of Molecular Genetics and Microbiology, College of Medicine, University of Florida, Gainesville, FL 32610.

Publisher

Mary Ann Liebert Inc

Subject

Genetics,Molecular Biology,Molecular Medicine

Link

http://www.liebertpub.com/doi/pdf/10.1089/hum.2012.218

Reference63 articles.

1. VEGF delivery with retrogradely transported lentivector prolongs survival in a mouse ALS model

2. Systemic Gene Delivery in Large Species for Targeting Spinal Cord, Brain, and Peripheral Tissues for Pediatric Disorders

3. A placebo-controlled trial of insulin-like growth factor-I in amyotrophic lateral sclerosis

4. Expression of Vascular Endothelial Growth Factor and Its Receptors in the Central Nervous System in Amyotrophic Lateral Sclerosis

5. Gene therapy of the brain in the dog model of Hurler's syndrome

Cited by 35 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Intrathecal AAV9/AP4M1 gene therapy for hereditary spastic paraplegia 50 shows safety and efficacy in preclinical studies;Journal of Clinical Investigation;2023-05-15

2. AAV9/MFSD8 gene therapy is effective in preclinical models of neuronal ceroid lipofuscinosis type 7 disease;Journal of Clinical Investigation;2022-03-01

3. Gene therapy for ALS: A review;Molecular Therapy;2021-12

4. Intravenous delivery of adeno-associated viral gene therapy in feline GM1 gangliosidosis;Brain;2021-08-19

5. Gene Therapy in a Mouse Model of Niemann–Pick Disease Type C1;Human Gene Therapy;2021-06-01